NAF has launched a petition on Change.org calling on the FDA to prioritize treatment options for rare diseases with urgent unmet needs, including Spinocerebellar Ataxia (SCA).
SIGN THE PETITION
Polyglutamine expansion diseases, also known as CAG triplet repeat disorders, are a group of neurodegenerative diseases caused by extra glutamine repeats being added into proteins. This group includes SCA1, SCA2, SCA3, SCA6, SCA7, SCA17, Huntinton’s Disease (HD), Spinal and bulbar muscular atrophy (SBMA), and Dentatorubropallidoluysian atrophy (DRPLA).
For more information on polyglutamine expansion diseases, see our article categories on the subject.
Our generous donors help us fund promising Ataxia research and offer support services to people with Ataxia. Your gift today will help us continue to deliver on our mission to improve the lives of persons affected by Ataxia.
Join for FREE today! Become a part of the community that is working together to find a cure. As a member you will receive access to the latest Ataxia news with our e-newsletter and Generations publication.
