Thinking about joining a clinical trial but unsure what it really involves? The Weill Cornell Medicine Department of Genetic Medicine team will take you behind the scenes and give you an inside look at the research participant experience, with a focus on their Friedreich’s Ataxia (FA) gene therapy trial. Their expert coordinator will walk you through the essentials — study visits, travel support, costs (spoiler: none!), and what to expect at every step. You’ll also meet Dr. Ronald Crystal, gene therapy expert and Principal Investigator of this FA study, who will be available for any medical/science related questions.

AAVrh.10hFXN is an investigational therapy that is under evaluation and not approved by the FDA. Anyone considering participating in a clinical trial or trying a new medication should discuss the matter with their physician. NAF does not endorse or recommend any particular studies or treatment options.